Data highlight advancements across ElevateBio's targeted gene insertion platform, powered by retrotransposon and machine learning-optimized ...

What was achieved: Researchers corrected SCN1A mutations in mice using prime or base editing, reducing seizures and improving survival. Why it matters: These are the first demonstrations of directly ...

Before Baby KJ was six months old, doctors at Children’s Hospital of Philadelphia injected a gene-editing therapy built for ...

On April 14, 2026, the United States Food and Drug Administration (“FDA”) issued a draft guidance for sponsors seeking approval of human ...

Gene editing has emerged as a powerful approach for targeting the genetic causes of disease, but getting the editing machinery into the right cells efficiently, safely, and at the scale needed for ...

In 2018, Chinese scientist He Jiankui shocked the world when he revealed that he had created the first gene-edited babies. Using Crispr, he tweaked the genes of three human embryos in an attempt to ...

Joint Statement by Ralph J. Cicerone and Victor J. Dzau WASHINGTON -- The National Academy of Sciences and the National Academy of Medicine are launching a major initiative to guide decision making ...

Humans have become very good at altering the basic building blocks of life to their advantage. Genetically modified foods are available at most grocery stores. Researchers use gene-editing tools every ...

When you think of the “Make America Healthy Again” (MAHA) movement, you might picture fertile soil, organic farms, and homeopathic remedies. For some, that vision is a welcome change; for others, it ...