CRISPR gene therapy Casgevy can nearly eliminate sickle cell crises, but difficult stem‑cell collection is delaying access ...

Sickle cell anemia (HbSS) is the homozygous dominant variant and the most common and severe form of the disease. Whereas patients who only inherited one gene encoding for abnormal HbS and a different ...

The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are ...

Opportunities in the Sickle Cell Disease market include advancing gene-editing therapies like EDIT-301, expanding VOC-reducing treatments such as inclacumab, and exploring novel drug candidates like ...

Avascular necrosis is the breakdown and death of bone tissue due to insufficient blood supply. It’s a common complication of sickle cell disease, but early diagnosis and treatment can help slow ...

Please provide your email address to receive an email when new articles are posted on . Researchers observed what they called “alarming” underutilization of disease-modifying therapies for sickle cell ...

A breakthrough study led by researchers at the University of Minnesota could explain why patients with the same genetic sickle cell mutation ...

What you need to know: Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease A biotechnology company in Uganda has developed a new ...