A high school senior channeled the loss of her murdered sister into academic success by earning valedictorian and acceptance ...

Near-term, we have the potential to transform the treatment of thalassemia and sickle cell disease with PYRUKYND. And beyond, we have the opportunity to deliver additional medicines to rare disease ...

New molecular entities (NMEs) are produced at the same rate today as they were 50 years ago. The industry has averaged one NME per company every 6 years, and its most successful firms have averaged ...

Apr. 7, 2026 A gene called KLF5 may be a key force behind the spread of pancreatic cancer—but not in the way scientists expected. Rather than mutating DNA, it rewires how genes are turned on and off, ...